Our Pipeline
BLUE GEN’S PIPELINE
BGTF-027 PROGRAM HIGHLIGHTS
- BGTF-027 is an intravitreal (IVT) gene therapy solution designed to deliver a functional copy of human L-opsin gene to the cone photoreceptors cells
- Non-surgical IVT delivery aims to preserve the fragile retina of BCM patients
- Robust IND-enabling package
- Successful FDA interactions
- Granted Orphan Drug Designation, ODD for ADVM-062 for the treatment of BCM
- Clinical drug supply secured